Patient advocacy groups are awaiting clarification on whether specific conditions will be covered by the National Policy of Rare Disorders (NPRD) 2021. This comes after the Union government recently allowed patients to receive treatment for six rare diseases by including…
Tag: Pharma News
The Rho kinase (ROCK) inhibitor NRL-1049, a potential treatment for people with cerebral cavernous malformations (CCM), a condition marked by abnormally enlarged capillary cavities in the brain and spinal cord, was dosed in the first two cohorts of the investigational…
Moderna, Inc., a biotechnology company that invented messenger RNA (mRNA) therapeutics and vaccines, and Generation Bio Co., a biotechnology company developing genetic medicines for people with common and rare diseases, recently announced that they have formed a strategic partnership to…
Tofersen, an investigational antisense drug for the treatment of people with superoxide dismutase 1 (SOD1) amyotrophic lateral sclerosis, was discussed at the Peripheral and Central Nervous System Drugs Advisory Committee meeting by the US Food and Drug Administration (FDA), according…
When concerns about drug resistance arise, Indian healthcare practitioners and pharmaceutical corporations step up their efforts to control the spread of tuberculosis through early identification and research for new medications. TB poses a serious risk to public health, with an…
The US Food and Drug Administration (FDA) has designated NTLA-2002 for the treatment of hereditary angioedema as a Regenerative Medicine Advanced Treatment (RMAT), according to Intellia Therapeutics, Inc., a leading clinical-stage genome editing business (HAE). NTLA-2002 is a CRISPR-based in…
The draught consensus statement for the treatment of urinary bladder cancer has been made public by the Indian Council of Medical Research (ICMR). Over a period of four weeks, from March 17 to April 14, 2023, the ICMR expert group’s…
The Central Government is taking a stand that the sale of medicines should strictly adhere to the provisions of the existing regulations and that the State Licensing Authorities (SLAs) are legally empowered to act against violations of the legal provisions….
A medical technology business called NeuroOne Medical Technologies Corporation said that the first animal implant of its innovative thin-film paddle leads for spinal cord stimulation had been successfully completed. The devices are designed to treat individuals with numerous failed back…
The FDA provided encouraging input on Kuria Therapeutics’ development plan for KTX-1161 for corneal endothelial dysfunction during a pre-Investigational New Drug (IND) interaction, according to the pharmaceutical company, which is working on innovative ophthalmic and dermal treatments. A topical ophthalmic…